1340. Lentiviral Vectors for In Vivo Gene Therapy of Metachromatic Leukokystrophy: Study on the Mechanisms Underlying the Therapeutic Effect

1340. Lentiviral Vectors for In Vivo Gene Therapy of Metachromatic Leukokystrophy: Study on the Mechanisms Underlying the Therapeutic Effect

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1339. Ribozyme-Mediated Striatal Reduction of Huntingtin in Adult Mice Edgardo Rodriguez,1 Lorraine Hamilton,2 Eileen Denovan-Wright,2 Alfred S. Lewin,3 Ronald J. Mandel.1 1 Neuroscience, University of Florida College of Medicine, Gainesville, FL, United States; 2Pharmacology, Dalhousie University, Halifax, Nova Scotia, Canada; 3Molecular Genetics, University of Florida College of Medicine, Gainesville, FL, United States. C     -C$/      

   

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Molecular Therapy Vol. 5, No. 5, May 2002, Part 2 of 2 Parts Copyright © The American Society of Gene Therapy

1340. Lentiviral V ectors for In V ivo Gene Therapy of Vectors Vivo Metachromatic Leukokystrophy: Study on the Mechanisms Underlying the Therapeutic Effect Antonella Consiglio,1 Diego Dolcetta,1 Tonia Luca,1 Alessandra Biffi,1 Angela Gritti,2 Antonia Follenzi,3 Angelo Vescovi,2 M. Grazia Roncarolo,1 Luigi Naldini,3 Claudio Bordignon.1 1 San Raffaele-Telethon Institute for Gene Therapy, (H.S.R.TIGET), Scientific Institute H. San Raffaele, Milan, Italy; 2Stem Cell Research Institute, Scientific Institute H. San Raffaele, Milan, Italy; 3Institute for Cancer Research and Treatment, University of Torino, Italy. #   D      -#D$/          

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