1210. Retroviral Gene Transfer of the WASP Gene to Lymphoblastoid B Cells of Wiskott-Aldrich Syndrome Patients. Evaluation of Phenotypic Correction

1210. Retroviral Gene Transfer of the WASP Gene to Lymphoblastoid B Cells of Wiskott-Aldrich Syndrome Patients. Evaluation of Phenotypic Correction

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1209. Functional Analysis of an Insulated Oncoretrovirus V ector for Human Gamma-Globin in Vector Mouse Models for Beta Thalassemia Tamon Nishino,1 Evangelia Yannaki,2 Julie Tubb,1 Qiliang Li,1 George Stamatoyannopoulos,1 David W. Emery.1 1 Department of Medicine, University of Washington, Seattle, WA, United States; 2Hematology /BMT Unit, G. Papanikolaou General Hospital, Thessaloniki, Greece. 0        

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3  @2 -M6/               @2  -=:±98389B% ,B±88389B%      B9±8:389B%     /     -B;±9, %    6;±85 %      Molecular Therapy Vol. 5, No. 5, May 2002, Part 2 of 2 Parts Copyright © The American Society of Gene Therapy

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1210. Retroviral Gene T ransfer of the W ASP Gene to Transfer WASP Lymphoblastoid B Cells of Wiskott-Aldrich Syndrome Patients. Evaluation of Phenotypic Correction Nuria Andreu,1,2 Josep M. Aran,1 Xavier Estivill,1,2 Cristina Fillat.1,2 1 Centre de Genetica Medica i Molecular, Institut de Recerca Oncològica, Hospitalet de Llobregat, Barcelona, Spain; 2 Programa Gens i Malaltia, Centre de Regulació Genòmica, Barcelona, Barcelona, Spain. 0 "'      -0'(/    F"

      

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121 1. Gene Therapy of Fanconi Anemia Groups A and 1211. C by Lentiviral V ectors Using Mouse as an Experimental Vectors Model: Comparison with Retroviral V ectors Vectors Meenakshi Noll,1 Francesco Galimi,2 Yoshiyuki Kanazawa,2 Timothy Lax,1 Alan D′Andrea,3 Inder Verma,2 Markus Grompe.1 1 Molecular and Medical Genetics, Oregon Health Sciences University, Portland, Oregon, United States; 2Genetics, The Salk Institute, La Jolla, California, United States; 3Pediatric Oncology, Dana-Farber Cancer Institute, Boston, MA, United States. ? '  -?'/               G

        

           

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