1217. Amelioration of Murine β-thalassemia Following Stem Cell Gene Transfer with a Human γ-Globin Lentiviral Vector

1217. Amelioration of Murine β-thalassemia Following Stem Cell Gene Transfer with a Human γ-Globin Lentiviral Vector

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1215. Retroviral Mediated T ransfer of Ankyrin 2.2 to Transfer nb/nb Spherocytosis Mutants and Engraftment in W/Wv Recipients Results in a New Hemolytic Anemia with Markedly Distorted Red Cell Shape Pamela S. Becker,1 Gerri J. Dooner,1 Helen M. Valinski,1 Berri Jacque,1 Patrick G. Gallagher,3 Bernard G. Forget,3 Jane E. Barker.2 1 Div. of Gene Therapy, Dept. of Medicine, Univ. of Massachusetts Med. School, Worcester, MA, United States; 2The Jackson Laboratory, Bar Harbor, ME, United States; 3Hematology Sect., Dept. of Int. Medicine, Yale Univ. Sch. of Medicine, New Haven, CT, United States.                                        

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Molecular Therapy Vol. 5, No. 5, May 2002, Part 2 of 2 Parts Copyright © The American Society of Gene Therapy

                   

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!" " 1216. Hematopoietic Stem Cells-Directed Gene Therapy: Chronic Granulomatous Disease Maciej Wiznerowicz, Didier Trono. 1 Genetics and Microbiology, University of Geneva, Geneva, Switzerland. C        -C( /               

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1217. Amelioration of Murine β-thalassemia Following Stem Cell Gene T ransfer with a Human γ-Globin Lentiviral Transfer Vector Derek A. Persons,1 Phillip W. Hargrove,1 Esther R. Allay,1 Hideki Hanawa,1 Arthur W. Nienhuis.1 1 Division of Experimental Hematology, St. Jude Children′s Research Hospital, Memphis, TN, United States. )            

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1218. Restoration of Correct Splicing by LentivirusDelivered SnRNAs in Cells Expressing β-thalassemic Pre-mRNAs Marla M. Vacek,1 Hong Ma,2 Tal Kafri,2 Ryszard Kole.1,3 1 Curriculum in Genetics and Molecular Biology, University of North Carolina at Chapel Hill, Chapel Hill, NC, United States; 2 Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC, United States; 3Lineberger Cancer Center, University of North Carolina at Chapel Hill, Chapel Hill, NC, United States.        β"         B&6 ;9&  ;6&           β"           &′             =′                 ,    

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1219. T reatment of Canine Cyclic Neutropenia by Treatment Lentivirus-Mediated G-CSF Delivery William R. Osborne,1 Ofer Yanay,1 Simon C. Barry,1 Louis J. Katen,1 Margaret Brzezinski,1 Lisa Y. Flint,1 Jeff Christensen,2 David C. Dale.2 1 Pediatrics, University of Washington, Seattle, WA, United States; 2 Medicine, University of Washington, Seattle, WA, United States.                                     G

                         

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1220. Phenotypic Correction of Fanconi Anemia Group A Hematopoietic Stem Cells Using Lentiviral V ectors Vectors Kaoru Yamada,1 Ali Ramezani,2 Robert G. Hawley,2 Wolfman Ebell,3 Fre Arwert,4 Christopher E. Walsh.1 1 Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC, United States; 2Holland Laboratory, American Red Cross, Rockville, MD, United States; 3Department of Hematology and Bone Marrow Transplantation, Charite Hospital, Berlin, Germany; 4Department of Human Genetics, Free University, Amsterdam, Netherlands. ? '  -?'*/               G

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Molecular Therapy Vol. 5, No. 5, May 2002, Part 2 of 2 Parts Copyright © The American Society of Gene Therapy