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34. Neonatal Delivery of a Retroviral Vector Expressing Canine β-Glucuronidase to the Liver Markedly Ameliorates the Clinical Manifestations of Mucopolysaccharidosis VII in Mice
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34. Neonatal Delivery of a Retroviral V ector Vector Expressing Canine β-Glucuronidase to the Liver Markedly Ameliorates the Clinical Manifestations of Mucopolysaccharidosis VII in Mice Robert L. Mango,1 Lingfei Xu,1,2 Mark S. Sands,1,3 Alex Hofling,1 Mark E. Haskins,4 Katherine P. Ponder.1,2 1 Internal Medicine, Washington University, St. Louis, MO, United States; 2Biochemistry and Molecular Biophysics, Washington University, St. Louis, MO, United States; 3Genetics, Washington University, St. Louis, MO, United States; 4Pathobiology, University of Pennsylvania School of Veterinary Medicine, Philadelphia, PA, United States. D
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34. Neonatal Delivery of a Retroviral V ector Vector Expressing Canine β-Glucuronidase to the Liver Markedly Ameliorates the Clinical Manifestations of Mucopolysaccharidosis VII in Mice Robert L. Mango,1 Lingfei Xu,1,2 Mark S. Sands,1,3 Alex Hofling,1 Mark E. Haskins,4 Katherine P. Ponder.1,2 1 Internal Medicine, Washington University, St. Louis, MO, United States; 2Biochemistry and Molecular Biophysics, Washington University, St. Louis, MO, United States; 3Genetics, Washington University, St. Louis, MO, United States; 4Pathobiology, University of Pennsylvania School of Veterinary Medicine, Philadelphia, PA, United States. D
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