563. Molecular Response to AAV or Plasmid-DNA Transduction of Human Skeletal Muscle

563. Molecular Response to AAV or Plasmid-DNA Transduction of Human Skeletal Muscle

!" "  ! 560. Integration of Recombinant SV40 V ectors and Vectors erm T ransgene Expression Term Transgene Long T David...

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560. Integration of Recombinant SV40 V ectors and Vectors erm T ransgene Expression Term Transgene Long T David S. Strayer,1 Francisco Branco,1 Mark A. Zern,2 Priscilla Yam,3 Sandra Calarotta,1 Carmen Nichols,1 John A. Zaia,3 John Rossi,3 Siddhartha Ghosh,4 Jayanta R. Chowdhury.4 1 Pathology, Jefferson Medical College, Philadelphia, Pennsylvania, United States; 2Medicine, University of California, Davis, Sacramento, California, United States; 3Virology and Molecualr Biology, Beckman Research Institute, City of Hope, Duarte, California, United States; 4Medicine, Albert Einstein College of Medicine, Bronx, New York, United States.   7 #               1  "       3           $*' @  "  

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561. Evaluation of AA VV ectors Based on Serotypes AAV Vectors 1,2 and 5 in Non-Human Primate Muscle, Liver and Retina Guang-Ping Gao,1,2 Alberto Auricchio,1,2 Lili Wang,1,2 Julie Johnston,1,2 Dana Hammill,1,2 Steven E. Raper,3 Rebecca Grant,1,2 Jean Bennett,4 James M. Wilson.1,2 1 Institute for Human Gene Therapy, University of Pennsylvania, Philadelphia, PA, United States; 2Wistar Institute, Philadelphia, PA, United States; 3Department of Surgery, University of Pennsylvania, Philadelphia, PA, United States; 4Department of Ophthalmology, University of Pennsylvania, Philadelphia, PA, United States. .      

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562. Mechanism of AA VT ransport into the CNS : A AAV Transport New Gene Therapy Route for Motor Neuron Diseases Elise Flavigny,1 Anna Salvetti,2 François Lachapelle,3 Pierre Bougnères,1 Patrick Aubourg,1 Nathalie Cartier.1 1 INSERM U342, Paris, France; 2Laboratoire de Thérapie Génique, Nantes, France; 3INSERM U546, Paris, France. ?                             

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563. Molecular Response to AA V or Plasmid-DNA AAV Transduction of Human Skeletal Muscle Joerg Schuettrumpf,1 Katherine A. High,1 Valder R. Arruda.1 1 Pediatrics, The Children′s Hospital of Philadelphia, University of Pennsylvania School of Medicine, Philadelphia, PA, United States. 4   " 

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564. Receptor-T argeted Adeno-Associated V irus Receptor-Targeted Virus (AA V) V ectors for Efficient Gene Delivery to Ovarian (AAV) Vectors Cancer Cell Lines and to a Xenograft Model of Human Ovarian Carcinoma Wenfang Shi, Jeffrey S. Bartlett. )               ′          '               



 

                                                               

                        

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565. Double Stranded AA V Offers Far More Than AAV Doubled Gene T ransfer Transfer Zhong Wang,1 Hsin-i Ma,1 Liangwu Sun,1 Jian Zhang,1 Juan Li,1 Xiao Xiao.1 1 Department of Molecular Genetics and Biochemistry, University of Pittsburgh School of Medicine, Pittsburgh, Pennsylvania, United States. ' " 

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